I'm in tears watching the slides. The 3 drugs combo gets in vitro CFTR function to 75% function. Orkambi only to 25%. Kalydeco...that miracle for 551...only got CFTR function to 50%. And for heterozygotes to almost 50%, which again is what Kalydeco did for 551!
vrtx.com has link if you want to watch, listen
Vertex Conference Live Now--triple combo gets up to 75% function
vrtx.com has link if you want to watch, listen
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